| USAN | Research Code | Structure | Drug Class | Therapeutic class | Target |
| actoxumab | MDX-066 | | monoclonal antibody | therapeutic | Clostridium difficile toxin A |
| bezlotoxumab | MDX-1388 | | monoclonal antibody | therapeutic | Clostridium difficile toxin B |
| migalastat | AT-1001, GR-181314A |  | natural product derived small molecule | therapeutic | alpha-galactosidase A |
| radium Ra 223 dichloride | BAY-88-8223 | RaCl2 | inorganic | radiopharmaceutical | n/a |
| surotomycin | CB-183,315 |  | natural product derived small molecule | therapeutic |
n/a |
| treprostinil diolamine | UT-15C |  | natural product derived small molecule | therapeutic | prostaglandin I2 receptor |